Gene Therapy Strategies for Duchenne Muscular Dystrophy Utilizing Recombinant Adeno-associated Virus Vectors: Molecular Therapy
Background of the disease - Exon skipping
What Causes Duchenne Muscular Dystrophy (DMD)?
Prenatal diagnosis of Duchenne muscular dystrophy revealed a novel mosaic mutation in Dystrophin gene: a case report | BMC Medical Genetics | Full Text
Evaluating the potential of novel genetic approaches for the treatment of Duchenne muscular dystrophy | European Journal of Human Genetics
DMD Gene(Dystrophin) - DMD ORF clone | GenScript
Duchenne muscular dystrophy | Nature Reviews Disease Primers
Dystrophin
The importance of genetic diagnosis for Duchenne muscular dystrophy | Journal of Medical Genetics
The Role of Genetics in Duchenne Muscular Dystrophy (DMD) | Duchenne.com
What Causes Duchenne Muscular Dystrophy (DMD)?
New gene editing strategies developed for Duchenne muscular dystrophy : Newsroom - UT Southwestern, Dallas, Texas
Dystrophin and mutations: one gene, several proteins, multiple phenotypes - The Lancet Neurology
Genetic Causes - Parent Project Muscular Dystrophy
Inheritance - Parent Project Muscular Dystrophy
Dystrophin isoforms and their expression
Full article: Gene therapy for Duchenne muscular dystrophy: an update on the latest clinical developments
DMD » Laboratory Testing and Research
In vivo genome editing in mouse restores dystrophin expression in Duchenne muscular dystrophy patient muscle fibers | Genome Medicine | Full Text
eDystrophin - Knowledge
Causes/Inheritance - Duchenne Muscular Dystrophy (DMD) - Diseases | Muscular Dystrophy Association
MDA2022 – DMD Gene Therapy PF-06939926 Safe at High Dose in Trial
Dystrophin and the two related genetic diseases, Duchenne and Becker muscular dystrophies - BiomolBiomed Viewpoints
Genes | Free Full-Text | Therapeutic Strategies for Duchenne Muscular Dystrophy: An Update
Toward the correction of muscular dystrophy by gene editing | PNAS
Blog: Why 7 and 9 are the magic numbers for World Duchenne Awareness Day | UON
Exons 45–55 Skipping Using Mutation-Tailored Cocktails of Antisense Morpholinos in the DMD Gene - ScienceDirect
